https://phys.org/news/2018-05-rna-modifying-tool-genetic-diseases-driver.html

Disney's deletion tool opens the possibility of creating drugs that can be taken conveniently as pills to correct genetic diseases—by destroying toxic gene products, and by chemically controlling the body's defense mechanisms. The paper, "Small molecule targeted recruitment of a nuclease to RNA," was published online by the Journal of the American Chemical Society.

"These studies, like much science, were about a decade in the making. We are very excited to see how this initial application evolves," Disney says. "This research further shows that RNA is indeed a viable target to make medicines."