Takeaways from AP's report on access to gene therapies for rare diseases
https://apnews.com/article/gene-therapy-wiskott-aldrich-rare-disease-79dac8beaa5e56d895e270cde430d0f1
The promise of gene therapy looms large for families dealing with rare, genetic disorders. Such treatments offer the possibility of one-time cures.
But families and researchers worry such therapies will remain out of reach.
