Gene-editing treatment shows promise for sickle cell disease
https://apnews.com/427c96de16a7a7481356054f6a97e5d3
Scientists are seeing promising early results from the first studies testing gene editing for painful, inherited blood disorders that plague millions worldwide.
Doctors hope the one-time treatment, which involves permanently altering DNA in blood cells with a tool called CRISPR, may treat and possibly cure sickle cell disease and beta thalassemia.